A patient and family perspective on gene therapy for rare diseases.
نویسندگان
چکیده
The authors describe the view of patients and patient organisations on gene therapy research and gene therapy regulations. In particular, the added value of partnership between scientists and patient organisations, and patient involvement in the gene therapy field, are addressed.
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ورودعنوان ژورنال:
- The journal of gene medicine
دوره 9 10 شماره
صفحات -
تاریخ انتشار 2007